Science

Therapeutic Focus Areas

  • Alpha-1 Antitrypsin Deficiency

    Alpha-1 Antitrypsin Deficiency

    Committed to Alpha-1 Patients

    Alpha-1 antitrypsin deficiency (AATD) is the most common hereditary disorder in adults. It is associated with an increased risk of developing pulmonary emphysema and liver disease, and also skin problems (panniculitis) and vasculitis.

  • COVID-19

    COVID-19

    Taking part in the fight against COVID-19

    Over the past months, our lives have changed dramatically as a result of the Coronavirus (COVID-19) pandemic. COVID-19 is caused by the novel virus SARS-CoV-2. As new facts about the virus and the pandemic are revealed, the international scientific community, along with the pharmaceutical industry, are making tremendous efforts in order to combat the disease. […]

  • Graft Versus Host Disease

    Graft Versus Host Disease

    Fighting Against GVHD

    The allogeneic transplantation of hematopoietic cells (HCT) is a well-established treatment for hematologic diseases that cannot be cured with conventional treatments.The most common life-threatening complication is Graft Versus Host Disease (GVHD).

  • Lung Transplantation

    Lung Transplantation

    Advancing a novel clinical program to prevent lung rejection

    A lung transplant is a surgical procedure to replace a diseased or failing one or both lungs with a healthy lung, usually from a deceased donor. A lung transplant is reserved for people who have tried other medications or treatments, but their conditions haven’t sufficiently improved. The donor lungs must be disease-free and matched as […]

  • Rabies

    Rabies

    Helping to prevent one of the deadliest diseases in the world

    Rabies is a preventable infectious viral disease that is almost always fatal following the onset of clinical symptoms. In up to 99% of cases, domestic dogs are responsible for rabies virus transmission to humans. Yet, rabies can affect both domestic and wild animals. It is spread to people through bites or scratches, usually via saliva. […]